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Nakamori Masayuki  中森 雅之

… Alternative Names

NAKAMORI Masayuki  中森 雅之

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Researcher Number 60630233
Other IDs
  • ORCIDhttps://orcid.org/0000-0003-4714-3044
Affiliation (Current) 2025: 山口大学, 大学院医学系研究科, 教授
2025: 大阪大学, 大学院医学系研究科, 特任准教授
Affiliation (based on the past Project Information) *help 2022 – 2024: 山口大学, 大学院医学系研究科, 教授
2021 – 2022: 大阪大学, 大学院医学系研究科, 特任准教授
2019 – 2021: 大阪大学, 医学系研究科, 特任准教授(常勤)
2019: 大阪大学, 医学(系)研究科, 特任講師
2018 – 2019: 大阪大学, 医学系研究科, 特任講師(常勤) … More
2016 – 2018: 大阪大学, 医学系研究科, 助教
2016: 大坂大学, 医学研究科, 特任助教
2016: 大阪大学, 大学院医学系研究科, 講師
2014 – 2016: 大阪大学, 医学(系)研究科(研究院), 助教
2015: 大阪大学, 医学研究科, 特任助教
2013: 大阪大学, 医学(系)研究科(研究院), 特任助教(常勤)
2013: 大阪大学, 医学部附属病院, その他
2012: 大阪大学, 医学部附属病院, 医員 Less
Review Section/Research Field
Principal Investigator
Neurology / Basic Section 52020:Neurology-related / Medium-sized Section 52:General internal medicine and related fields
Except Principal Investigator
Nerve anatomy/Neuropathology / Chemistry / Science and Engineering
Keywords
Principal Investigator
トリプレットリピート / 筋強直性ジストロフィー / ハンチントン病 / 核酸標的低分子 / 脊髄小脳失調症 / リピート不安定性 / DNA修復 / トリプレットリピート病 / 歯状核赤核淡蒼球ルイ体萎縮症 / DRPLA … More / 低分子化合物 / RNA毒性 / スプライシング / 核酸医薬 / 脊髄小脳萎縮症 / リピート病 / CTGリピート / CAGリピート / 脊髄小脳変性症 / ミスマッチ修復 … More
Except Principal Investigator
クロマチン構造 / 疾患特異的iPS細胞 / CTGリピート / iPS細胞 / CTGリピート伸長 / 筋強直性ジストロフィー / 患者由来iPS細胞 / 病態再現 / プロープ / RNA機能調節 / 伸長抑制 / プローブ / 小分子 / 分子合成 / スクリーニング / 分子設計 / 遺伝子疾患 / 低分子 / 毒性RNA / 神経変性疾患 / 核酸結合低分子 / トリヌクレオチドリピート Less
  • Research Projects

    (8 results)
  • Research Products

    (206 results)
  • Co-Researchers

    (20 People)
  •  トリプレットリピート病のリピート長変動機構解明とリピート短縮治療の基盤確立Principal Investigator

    • Principal Investigator
      中森 雅之
    • Project Period (FY)
      2021 – 2025
    • Research Category
      Grant-in-Aid for Scientific Research (B)
    • Review Section
      Basic Section 52020:Neurology-related
    • Research Institution
      Yamaguchi University
      Osaka University
  •  Developing a treatment for trinucleotide repeat expansion disorders through repeat shorteningPrincipal Investigator

    • Principal Investigator
      Nakamori Masayuki
    • Project Period (FY)
      2019 – 2023
    • Research Category
      Grant-in-Aid for Challenging Research (Exploratory)
    • Review Section
      Medium-sized Section 52:General internal medicine and related fields
    • Research Institution
      Yamaguchi University
      Osaka University
  •  Therapeutic developemt for myotonic dystrophyPrincipal Investigator

    • Principal Investigator
      Nakamori Masayuki
    • Project Period (FY)
      2016 – 2020
    • Research Category
      Grant-in-Aid for Scientific Research (B)
    • Research Field
      Neurology
    • Research Institution
      Osaka University
  •  Allele specific inhibition of mutant mRNA expression for repeat expansion disordersPrincipal Investigator

    • Principal Investigator
      Nakamori Masayuki
    • Project Period (FY)
      2015 – 2018
    • Research Category
      Grant-in-Aid for Challenging Exploratory Research
    • Research Field
      Neurology
    • Research Institution
      Osaka University
  •  Chemical Biology Studies on Trinucleotide Repeat Disease using Repeat-Binding Molecules

    • Principal Investigator
      NAKATANI Kazuhiko
    • Project Period (FY)
      2014 – 2019
    • Research Category
      Grant-in-Aid for Specially Promoted Research
    • Review Section
      Science and Engineering
      Chemistry
    • Research Institution
      Osaka University
  •  Myotonic dystrophy type 1 patient-derived iPSCs for the investigation of CTG repeat instability

    • Principal Investigator
      SAKURAI Hidetoshi
    • Project Period (FY)
      2014 – 2016
    • Research Category
      Grant-in-Aid for Scientific Research (C)
    • Research Field
      Nerve anatomy/Neuropathology
    • Research Institution
      Kyoto University
  •  Modulation of repeat size in trinucleotide repeat expansion disordersPrincipal Investigator

    • Principal Investigator
      NAKAMORI Masayuki
    • Project Period (FY)
      2013 – 2016
    • Research Category
      Grant-in-Aid for Young Scientists (A)
    • Research Field
      Neurology
    • Research Institution
      Osaka University
  •  トリプレットリピート病におけるリピート伸長機構の解明と制御Principal Investigator

    • Principal Investigator
      中森 雅之
    • Project Period (FY)
      2012 – 2013
    • Research Category
      Grant-in-Aid for Research Activity Start-up
    • Research Field
      Neurology
    • Research Institution
      Osaka University

All 2024 2023 2022 2021 2020 2019 2018 2017 2016 2015 2014 2013 Other

All Journal Article Presentation Book Patent

  • [Book] 新臨床内科学 第10版2020

    • Author(s)
      中森雅之
    • Total Pages
      2
    • Publisher
      医学書店
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Book] 内科学書 改訂第9版2019

    • Author(s)
      中森雅之
    • Total Pages
      5
    • Publisher
      中山書店
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Book] 内科学書 改訂第9版 筋強直症候群2019

    • Author(s)
      中森雅之
    • Total Pages
      5
    • Publisher
      中山書店
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Book] Translational research in muscular dystrophy2016

    • Author(s)
      Nakamori M, Takahashi MP.
    • Total Pages
      23
    • Publisher
      Springer Japan
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Book] Translational Research in Muscular Dystrophy: Myotonic Dystrophy2016

    • Author(s)
      Nakamori M, Takahashi MP.
    • Total Pages
      23
    • Publisher
      Springer
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Book] 筋疾患診療ハンドブック2013

    • Author(s)
      中森雅之, 高橋正紀
    • Publisher
      中外医学社
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Book] 筋疾患のみかた・考え方2013

    • Author(s)
      中森雅之
    • Total Pages
      6
    • Publisher
      中外医薬社
    • Data Source
      KAKENHI-PROJECT-24890110
  • [Book] 脳212013

    • Author(s)
      中森雅之
    • Total Pages
      7
    • Publisher
      金芳堂
    • Data Source
      KAKENHI-PROJECT-24890110
  • [Journal Article] Erythromycin for myotonic dystrophy type 1: a multicentre, randomised, double-blind, placebo-controlled, phase 2 trial2024

    • Author(s)
      Nakamori Masayuki、Nakatani Daisaku、Sato Tomoharu、Hasuike Yuhei、Kon Seiko、Saito Toshio、Nakamura Harumasa、Takahashi Masanori P.、Hida Eisuke、Komaki Hirofumi、Matsumura Tsuyoshi、Takada Hiroto、Mochizuki Hideki
    • Journal Title

      eClinicalMedicine

      Volume: 67 Pages: 102390-102390

    • DOI

      10.1016/j.eclinm.2023.102390

    • Peer Reviewed / Open Access
    • Data Source
      KAKENHI-PROJECT-21K11784, KAKENHI-PROJECT-19K22597
  • [Journal Article] Contribution of Complement, Microangiopathy and Inflammation in Idiopathic Inflammatory Myopathies2024

    • Author(s)
      Honda Masaya、Shimizu Fumitaka、Sato Ryota、Nakamori Masayuki
    • Journal Title

      Journal of Neuromuscular Diseases

      Volume: 11 Issue: 1 Pages: 5-16

    • DOI

      10.3233/jnd-230168

    • Peer Reviewed / Open Access
    • Data Source
      KAKENHI-PROJECT-21K07416, KAKENHI-PROJECT-19K22597
  • [Journal Article] Expanded‐repeat‐RNA‐mediated disease mechanisms in myotonic dystrophy2024

    • Author(s)
      Nakamori Masayuki
    • Journal Title

      Neurology and Clinical Neuroscience

      Volume: 12 Issue: 1 Pages: 16-23

    • DOI

      10.1111/ncn3.12687

    • Peer Reviewed
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Journal Article] Analysis of splicing abnormalities in the white matter of myotonic dystrophy type 1 brain using RNA sequencing2024

    • Author(s)
      Yoshizumi Kazuki、Nishi Masamitsu、Igeta Masataka、Nakamori Masayuki、Inoue Kimiko、Matsumura Tsuyoshi、Fujimura Harutoshi、Jinnai Kenji、Kimura Takashi
    • Journal Title

      Neuroscience Research

      Volume: 200 Pages: 48-56

    • DOI

      10.1016/j.neures.2023.10.002

    • Peer Reviewed
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Journal Article] Phase II/III Study of Aceneuramic Acid Administration for GNE Myopathy in Japan2023

    • Author(s)
      Suzuki Naoki、Mori-Yoshimura Madoka、Katsuno Masahisa、Takahashi Masanori P.、Yamashita Satoshi、Oya Yasushi、Hashizume Atsushi、Yamada Shinichiro、Nakamori Masayuki、Izumi Rumiko、Kato Masaaki、Warita Hitoshi、Tateyama Maki、Kuroda Hiroshi、Asada Ryuta、Yamaguchi Takuhiro、Nishino Ichizo、Aoki Masashi
    • Journal Title

      Journal of Neuromuscular Diseases

      Volume: - Issue: 4 Pages: 1-12

    • DOI

      10.3233/jnd-230029

    • Peer Reviewed / Open Access
    • Data Source
      KAKENHI-PROJECT-21K07411, KAKENHI-PROJECT-23K18260, KAKENHI-PROJECT-19K22597
  • [Journal Article] Efficacy confirmation study of aceneuramic acid administration for GNE myopathy in Japan2023

    • Author(s)
      Mori-Yoshimura Madoka、Suzuki Naoki、Katsuno Masahisa、Takahashi Masanori P.、Yamashita Satoshi、Oya Yasushi、Hashizume Atsushi、Yamada Shinichiro、Nakamori Masayuki、Izumi Rumiko、Kato Masaaki、Warita Hitoshi、Tateyama Maki、Kuroda Hiroshi、Asada Ryuta、Yamaguchi Takuhiro、Nishino Ichizo、Aoki Masashi
    • Journal Title

      Orphanet Journal of Rare Diseases

      Volume: 18 Issue: 1 Pages: 241-241

    • DOI

      10.1186/s13023-023-02850-y

    • Peer Reviewed / Open Access
    • Data Source
      KAKENHI-PROJECT-23K18260, KAKENHI-PROJECT-19K22597
  • [Journal Article] Deregulations of miR‐1 and its target Multiplexin promote dilated cardiomyopathy associated with myotonic dystrophy type 12023

    • Author(s)
      Souidi Anissa、Nakamori Masayuki、Zmojdzian Monika、Jagla Teresa、Renaud Yoan、Jagla Krzysztof
    • Journal Title

      EMBO reports

      Volume: 24 Issue: 4

    • DOI

      10.15252/embr.202256616

    • Peer Reviewed / Open Access / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Journal Article] Intracerebral Distribution of CAG Repeat-Binding Small Molecule Visualized by Whole-Brain Imaging2023

    • Author(s)
      Murakami Eitaro、Nakamori Masayuki、Nakatani Kazuhiko、Shibata Tomonori、Tainaka Kazuki
    • Journal Title

      Bioconjugate Chemistry

      Volume: 34 Issue: 12 Pages: 2187-2193

    • DOI

      10.1021/acs.bioconjchem.3c00470

    • Peer Reviewed
    • Data Source
      KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-21K19049, KAKENHI-PROJECT-22H00351, KAKENHI-PROJECT-23K24198
  • [Journal Article] 筋強直性ジストロフィーの中枢神経病態2023

    • Author(s)
      中森雅之
    • Journal Title

      Dementia Japan

      Volume: 37 Pages: 75-81

    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Journal Article] Antagonistic roles of canonical and Alternative-RPA in disease-associated tandem CAG repeat instability2023

    • Author(s)
      Gall-Duncan Terence、Luo Jennifer、Mehkary Mustafa、Sato Nozomu、Caron Marie-Christine、Panigrahi Gagan B.、Wang Peixiang、Lau Rachel、Masson Jean-Yves、Tippett Lynette、Turner Clinton、Spies Maria、Campos Eric I.、Faull Richard L.M.、Davidson Beverly L.、Nakamori Masayuki、et al.
    • Journal Title

      Cell

      Volume: 186 Issue: 22 Pages: 4898-4919

    • DOI

      10.1016/j.cell.2023.09.008

    • Peer Reviewed / Open Access / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-22H00464
  • [Journal Article] 筋強直性ジストロフィーの創薬開発2023

    • Author(s)
      中森雅之
    • Journal Title

      遺伝子医学

      Volume: 13 Pages: 16-22

    • Data Source
      KAKENHI-PROJECT-23K21411
  • [Journal Article] 筋強直性ジストロフィーの創薬開発2023

    • Author(s)
      中森雅之
    • Journal Title

      遺伝子医学

      Volume: 13 Pages: 16-22

    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Journal Article] 分子病態と先端治療開発ー筋強直性ジストロフィー2022

    • Author(s)
      中森雅之
    • Journal Title

      医学と薬学

      Volume: 79 Pages: 1177-1184

    • Data Source
      KAKENHI-PROJECT-23K21411
  • [Journal Article] Cellular Senescence and Aging in Myotonic Dystrophy2022

    • Author(s)
      Hasuike Yuhei、Mochizuki Hideki、Nakamori Masayuki
    • Journal Title

      International Journal of Molecular Sciences

      Volume: 23 Issue: 4 Pages: 2339-2339

    • DOI

      10.3390/ijms23042339

    • Peer Reviewed / Open Access
    • Data Source
      KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-19K17007, KAKENHI-PROJECT-23K21411
  • [Journal Article] 筋強直性ジストロフィーの治療開発と今後の展望2022

    • Author(s)
      中森雅之
    • Journal Title

      医療

      Volume: 76 Pages: 40-44

    • Data Source
      KAKENHI-PROJECT-23K21411
  • [Journal Article] Cell type-specific abnormalities of central nervous system in myotonic dystrophy type 12022

    • Author(s)
      Nakamori Masayuki、Shimizu Hiroshi、Ogawa Kotaro、Hasuike Yuhei、Nakajima Takashi、Sakurai Hidetoshi、Araki Toshiyuki、Okada Yukinori、Kakita Akiyoshi、Mochizuki Hideki
    • Journal Title

      Brain Communications

      Volume: 4 Issue: 3 Pages: 154-154

    • DOI

      10.1093/braincomms/fcac154

    • Peer Reviewed / Open Access
    • Data Source
      KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-23K21411
  • [Journal Article] Therapeutic approach for myotonic dystrophy: Recent advances in translational research2022

    • Author(s)
      Nakamori Masayuki
    • Journal Title

      Neurology and Clinical Neuroscience

      Volume: 10 Issue: 6 Pages: 334-339

    • DOI

      10.1111/ncn3.12499

    • Peer Reviewed
    • Data Source
      KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-23K21411
  • [Journal Article] 筋強直性ジストロフィー2022

    • Author(s)
      中森雅之
    • Journal Title

      医学のあゆみ

      Volume: 283 Pages: 971-977

    • Data Source
      KAKENHI-PROJECT-23K21411
  • [Journal Article] 筋強直性ジストロフィーの治療開発と今後の展望2022

    • Author(s)
      中森雅之
    • Journal Title

      医療

      Volume: 76 Pages: 40-44

    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Journal Article] 筋強直性ジストロフィー2022

    • Author(s)
      中森雅之
    • Journal Title

      医学のあゆみ

      Volume: 283 Pages: 971-977

    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Journal Article] 分子病態と先端治療開発ー筋強直性ジストロフィー2022

    • Author(s)
      中森雅之
    • Journal Title

      医学と薬学

      Volume: 79 Pages: 1177-1184

    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Journal Article] CAG repeat-binding small molecule improves motor coordination impairment in a mouse model of Dentatorubral?pallidoluysian atrophy2022

    • Author(s)
      Hasuike Yuhei、Tanaka Hana、Gall-Duncan Terence、Mehkary Mustafa、Nakatani Kazuhiko、Pearson Christopher E.、Tsuji Shoji、Mochizuki Hideki、Nakamori Masayuki
    • Journal Title

      Neurobiology of Disease

      Volume: 163 Pages: 105604-105604

    • DOI

      10.1016/j.nbd.2021.105604

    • Peer Reviewed / Open Access / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-19H00924, KAKENHI-PROJECT-23K21411
  • [Journal Article] Expanded CUG Repeat RNA Induces Premature Senescence in Myotonic Dystrophy Model Cells2022

    • Author(s)
      Hasuike Yuhei、Mochizuki Hideki、Nakamori Masayuki
    • Journal Title

      Frontiers in Genetics

      Volume: 13 Pages: 865811-865811

    • DOI

      10.3389/fgene.2022.865811

    • Peer Reviewed / Open Access
    • Data Source
      KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-19K17007, KAKENHI-PROJECT-23K21411
  • [Journal Article] 筋強直性ジストロフィーの治療法開発2021

    • Author(s)
      中森雅之
    • Journal Title

      神経治療学

      Volume: 38 Pages: 283-285

    • NAID

      130008142577

    • Data Source
      KAKENHI-PROJECT-23K21411
  • [Journal Article] 治療法の開発を見据えた筋強直性ジストロフィーの新たな病態の解明2021

    • Author(s)
      中森雅之
    • Journal Title

      生体の科学

      Volume: 72 Pages: 582-585

    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Journal Article] 神経疾患研究の現状の課題と展望(2)筋疾患2021

    • Author(s)
      青木吉嗣、中森雅之
    • Journal Title

      Clinical Neuroscience

      Volume: 39 Pages: 1296-1300

    • Data Source
      KAKENHI-PROJECT-23K21411
  • [Journal Article] FAN1 exo- not endo-nuclease pausing on disease-associated slipped-DNA repeats: A mechanism of repeat instability2021

    • Author(s)
      Deshmukh Amit Laxmikant、Caron Marie-Christine、Mohiuddin Mohiuddin、Lanni Stella、Panigrahi Gagan B.、Khan Mahreen、Engchuan Worrawat、Shum Natalie、Faruqui Aisha、Wang Peixiang、Yuen Ryan K.C.、Nakamori Masayuki、Nakatani Kazuhiko、Masson Jean-Yves、Pearson Christopher E.
    • Journal Title

      Cell Reports

      Volume: 37 Issue: 10 Pages: 110078-110078

    • DOI

      10.1016/j.celrep.2021.110078

    • Peer Reviewed / Open Access / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-19H00924, KAKENHI-PROJECT-19K22597
  • [Journal Article] シヌクレインを標的としたParkinson病治療の現状と展望2021

    • Author(s)
      中森雅之
    • Journal Title

      神経治療学

      Volume: 38 Pages: 325-328

    • NAID

      130008142748

    • Data Source
      KAKENHI-PROJECT-23K21411
  • [Journal Article] Alpha‐synuclein dynamics in induced pluripotent stem cell‐derived dopaminergic neurons from a Parkinson’s disease patient ( PARK4 ) with SNCA triplication2021

    • Author(s)
      Fukusumi Hayato、Togo Kazuyuki、Sumida Miho、Nakamori Masayuki、Obika Satoshi、Baba Kousuke、Shofuda Tomoko、Ito Daisuke、Okano Hideyuki、Mochizuki Hideki、Kanemura Yonehiro
    • Journal Title

      FEBS Open Bio

      Volume: 11 Issue: 2 Pages: 354-366

    • DOI

      10.1002/2211-5463.13060

    • Peer Reviewed / Open Access / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-18H02741, KAKENHI-PROJECT-18K07534, KAKENHI-PROJECT-23K21397
  • [Journal Article] 筋強直性ジストロフィーの治療法開発2021

    • Author(s)
      中森雅之
    • Journal Title

      神経治療学

      Volume: 38 Pages: 283-285

    • NAID

      130008142577

    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Journal Article] 治療法の開発を見据えた筋強直性ジストロフィーの新たな病態の解明2021

    • Author(s)
      中森雅之
    • Journal Title

      生体の科学

      Volume: 72 Pages: 582-585

    • Data Source
      KAKENHI-PROJECT-23K21411
  • [Journal Article] 筋強直性ジストロフィー2020

    • Author(s)
      中森雅之, 高橋正紀.
    • Journal Title

      小児科診療

      Volume: 83 Pages: 45-50

    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Journal Article] 筋強直性ジストロフィーの治療薬の開発2020

    • Author(s)
      中森雅之
    • Journal Title

      小児内科

      Volume: 52 Pages: 428-432

    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Journal Article] The dimeric form of 1, 3 - diaminoisoquinoline derivative rescued the mis - splicing of Atp2a1 and Clcn1 genes in myotonic dystrophy type 1 mouse model2020

    • Author(s)
      Matsumoto, J. ; Nakamori, M. ; Okamoto, T. ; Murata, A. ; Dohno, C. ; Nakatani, K.
    • Journal Title

      Chem. Eur. J.

      Volume: 26 Issue: 63 Pages: 14305-14309

    • DOI

      10.1002/chem.202001572

    • Peer Reviewed / Open Access
    • Data Source
      KAKENHI-PROJECT-26000007, KAKENHI-PROJECT-18K05355, KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-19H00924, KAKENHI-PROJECT-18H02107, KAKENHI-PROJECT-16H05321
  • [Journal Article] Targeting Expanded Repeats by Small Molecules in Repeat Expansion Disorders2020

    • Author(s)
      Nakamori Masayuki、Mochizuki Hideki
    • Journal Title

      Movement Disorders

      Volume: 36 Issue: 2 Pages: 298-305

    • DOI

      10.1002/mds.28397

    • Peer Reviewed
    • Data Source
      KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-16H05321
  • [Journal Article] 筋強直性ジストロフィーにおけるRNA毒性を標的とした治療戦略2020

    • Author(s)
      中森雅之
    • Journal Title

      実験医学

      Volume: 38 Pages: 2179-2185

    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Journal Article] A slipped-CAG DNA-binding small molecule induces trinucleotide-repeat contractions in vivo2020

    • Author(s)
      Nakamori Masayuki, Panigrahi Gagan B., Lanni Stella, et. al.
    • Journal Title

      Nature Genetics

      Volume: 52 Issue: 2 Pages: 146-159

    • DOI

      10.1038/s41588-019-0575-8

    • Peer Reviewed / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-18K05355, KAKENHI-PROJECT-19K07992, KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-26000007, KAKENHI-PROJECT-16H05321
  • [Journal Article] ミオトニア症候群2020

    • Author(s)
      中森雅之
    • Journal Title

      新臨床内科学 第10版

      Volume: 10 Pages: 1472-1473

    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Journal Article] 筋強直性ジストロフィーの治療薬の開発2020

    • Author(s)
      中森雅之
    • Journal Title

      小児内科

      Volume: 52 Pages: 428-32

    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Journal Article] 筋強直性ジストロフィーの医師主導治験2020

    • Author(s)
      中森雅之
    • Journal Title

      難病と在宅ケア

      Volume: 26 Pages: 13-16

    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Journal Article] Alternative splicing of clathrin heavy chain contributes to the switch from coated pits to plaques2020

    • Author(s)
      Moulay Gilles、Laine Jeanne、Lemaitre Magane、Nakamori Masayuki、Nishino Ichizo、Caillol Ghislaine、Mamchaoui Kamel、Julien Laura、Dingli Florent、Loew Damarys、Bitoun Marc、Leterrier Christophe、Furling Denis、Vassilopoulos Stephane
    • Journal Title

      Journal of Cell Biology

      Volume: 219 Issue: 9

    • DOI

      10.1083/jcb.201912061

    • Peer Reviewed / Open Access / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-16H05321
  • [Journal Article] 筋強直性ジストロフィー2020

    • Author(s)
      中森雅之, 高橋正紀
    • Journal Title

      小児科診療

      Volume: 83 Pages: 45-50

    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Journal Article] 筋強直性ジストロフィーにおけるRNA毒性を標的とした治療戦略2020

    • Author(s)
      中森雅之
    • Journal Title

      実験医学

      Volume: 38 Pages: 2179-2185

    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Journal Article] Modulating RNA secondary and tertiary structures by mismatch binding ligands2019

    • Author(s)
      Murata Asako、Nakamori Masayuki、Nakatani Kazuhiko
    • Journal Title

      Methods

      Volume: 167 Pages: 78-91

    • DOI

      10.1016/j.ymeth.2019.05.006

    • Peer Reviewed
    • Data Source
      KAKENHI-PROJECT-18K05355, KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-26000007, KAKENHI-PROJECT-16H05321
  • [Journal Article] The myotonic dystrophy health index: Japanese adaption and validity testing2019

    • Author(s)
      Mori Itsuki、Fujino Haruo、Matsumura Tsuyoshi、Takada Hiroto、Ogata Katsuhisa、Nakamori Masayuki、Innami Keisuke、Shingaki Honoka、Imura Osamu、Takahashi Masanori P.、Heatwole Chad
    • Journal Title

      Muscle & Nerve

      Volume: 印刷中 Issue: 5 Pages: 577-582

    • DOI

      10.1002/mus.26422

    • Peer Reviewed / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-15K15339, KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-17K14067, KAKENHI-PROJECT-16H05321
  • [Journal Article] Straightjacket/α2δ3 deregulation is associated with cardiac conduction defects in myotonic dystrophy type 1.2019

    • Author(s)
      Plantie E, Nakamori M, Renaud Y, Huguet A, Choquet C, Dondi C, Miquerol L, Takahashi M, Gourdon G, Junion G, Jagla T, Zmojdzian M, Jagla K
    • Journal Title

      eLife

      Volume: 8

    • DOI

      10.7554/elife.51114

    • Peer Reviewed / Open Access / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-19K07992, KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-16H05321
  • [Journal Article] A CTG repeat-selective chemical screen identifies microtubule inhibitors as selective modulators of toxic CUG RNA levels2019

    • Author(s)
      Reddy Kaalak、Jenquin Jana R.、McConnell Ona L.、Cleary John D.、Richardson Jared I.、Pinto Belinda S.、Haerle Maja C.、Delgado Elizabeth、Planco Lori、Nakamori Masayuki、Wang Eric T.、Berglund J. Andrew
    • Journal Title

      Proceedings of the National Academy of Sciences

      Volume: 116 Issue: 42 Pages: 20991-21000

    • DOI

      10.1073/pnas.1901893116

    • Peer Reviewed / Open Access / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-16H05321
  • [Journal Article] Nucleic Acid-Based Therapeutics for Parkinson's Disease.2019

    • Author(s)
      Nakamori M, Junn E, Mochizuki H, Mouradian MM.
    • Journal Title

      Neurotherapeutics

      Volume: 16 Issue: 2 Pages: 287-298

    • DOI

      10.1007/s13311-019-00714-7

    • Peer Reviewed / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-16H05321
  • [Journal Article] Amido-bridged nucleic acid (AmNA)-modified antisense oligonucleotides targeting α-synuclein as a novel therapy for Parkinson’s disease2019

    • Author(s)
      Uehara Takuya、Choong Chi-Jing、Nakamori Masayuki、Hayakawa Hideki、Nishiyama Kumiko、Kasahara Yuuya、Baba Kousuke、Nagata Tetsuya、Yokota Takanori、Tsuda Hiroshi、Obika Satoshi、Mochizuki Hideki
    • Journal Title

      Scientific Reports

      Volume: 9 Issue: 1 Pages: 7567-7567

    • DOI

      10.1038/s41598-019-43772-9

    • Peer Reviewed / Open Access
    • Data Source
      KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-18H02718, KAKENHI-PROJECT-16H05321
  • [Journal Article] Combination Treatment of Erythromycin and Furamidine Provides Additive and Synergistic Rescue of Mis-splicing in Myotonic Dystrophy Type 1 Models2019

    • Author(s)
      Jenquin Jana R.、Yang Hongfen、Huigens III Robert W.、Nakamori Masayuki、Berglund J. Andrew
    • Journal Title

      ACS Pharmacology & Translational Science

      Volume: 2 Issue: 4 Pages: 247-263

    • DOI

      10.1021/acsptsci.9b00020

    • Peer Reviewed / Open Access / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-16H05321
  • [Journal Article] Human Genomic Safe Harbors and the Suicide Gene‐Based Safeguard System for iPSC‐Based Cell Therapy2019

    • Author(s)
      Kimura Yasuyoshi、Shofuda Tomoko、Higuchi Yuichiro、Nagamori Ippei、Oda Masaaki、Nakamori Masayuki、Onodera Masafumi、Kanematsu Daisuke、Yamamoto Atsuyo、Katsuma Asako、Suemizu Hiroshi、Nakano Toru、Kanemura Yonehiro、Mochizuki Hideki
    • Journal Title

      STEM CELLS Translational Medicine

      Volume: 8 Issue: 7 Pages: 627-638

    • DOI

      10.1002/sctm.18-0039

    • Peer Reviewed / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-19K22597, KAKENHI-PROJECT-16H05321
  • [Journal Article] A Dimeric 2,9‐Diamino‐1,10‐phenanthroline Derivative Improves Alternative Splicing in Myotonic Dystrophy Type 1 Cell and Mouse Models2018

    • Author(s)
      Li Jinxing、Nakamori Masayuki、Matsumoto Jun、Murata Asako、Dohno Chikara、Kiliszek Agnieszka、Taylor Katarzyna、Sobczak Krzysztof、Nakatani Kazuhiko
    • Journal Title

      Chemistry - A European Journal

      Volume: 24 Issue: 68 Pages: 18115-18122

    • DOI

      10.1002/chem.201804368

    • Peer Reviewed / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-18K05355, KAKENHI-PROJECT-15K15339, KAKENHI-PROJECT-16H05321, KAKENHI-PROJECT-18H02107, KAKENHI-PROJECT-17J02038, KAKENHI-PROJECT-26000007
  • [Journal Article] 筋強直性ジストロフィーの病態と治療戦略2018

    • Author(s)
      中森雅之
    • Journal Title

      医学のあゆみ

      Volume: 267 Pages: 830-835

    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Journal Article] 筋強直性ジストロフィー2018

    • Author(s)
      中森雅之
    • Journal Title

      Clinical Neuroscience

      Volume: 36 Pages: 191-194

    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Journal Article] Furamidine Rescues Myotonic Dystrophy Type I Associated Mis-Splicing through Multiple Mechanisms2018

    • Author(s)
      Jenquin Jana R.、Coonrod Leslie A.、Silverglate Quinn A.、Pellitier Natalie A.、Hale Melissa A.、Xia Guangbin、Nakamori Masayuki、Berglund J. Andrew
    • Journal Title

      ACS Chemical Biology

      Volume: 13 Issue: 9 Pages: 2708-2718

    • DOI

      10.1021/acschembio.8b00646

    • Peer Reviewed / Open Access / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-15K15339, KAKENHI-PROJECT-16H05321
  • [Journal Article] 筋強直性ジストロフィーの病態と治療戦略2018

    • Author(s)
      中森雅之
    • Journal Title

      医学のあゆみ

      Volume: 267 Pages: 830-835

    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Journal Article] Macroscopic and microscopic diversity of missplicing in the central nervous system of patients with myotonic dystrophy type 12018

    • Author(s)
      Furuta M, Kimura T, Nakamori M, Matsumura T, Fujimura H, Jinnai K, Takahashi MP, Mochizuki H, Yoshikawa H.
    • Journal Title

      Neuroreport

      Volume: 29 Issue: 3 Pages: 235-240

    • DOI

      10.1097/wnr.0000000000000968

    • Peer Reviewed
    • Data Source
      KAKENHI-PROJECT-15K15339, KAKENHI-PROJECT-16H05321
  • [Journal Article] 筋強直性ジストロフィー2018

    • Author(s)
      中森雅之
    • Journal Title

      Clinical Neuroscience

      Volume: 36 Pages: 191-194

    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Journal Article] パーキンソン病の新展開ー核酸治療2017

    • Author(s)
      中森雅之, 望月秀樹.
    • Journal Title

      医学のあゆみ

      Volume: 262 Pages: 683-687

    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Journal Article] Disrupted prenatal RNA processing and myogenesis in congenital myotonic dystrophy2017

    • Author(s)
      Thomas James D.、Sznajder ?ukasz J.、Bardhi Olgert、Aslam Faaiq N.、Anastasiadis Zacharias P.、Scotti Marina M.、Nishino Ichizo、Nakamori Masayuki、Wang Eric T.、Swanson Maurice S.
    • Journal Title

      Genes Dev

      Volume: 31 Issue: 11 Pages: 1122-1133

    • DOI

      10.1101/gad.300590.117

    • Peer Reviewed / Open Access / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-15K15339, KAKENHI-PROJECT-16H05321
  • [Journal Article] Myotonic Dystrophy: Advances in Translational Research2017

    • Author(s)
      Nakamori M, Takahashi MP.
    • Journal Title

      BRAIN and NERVE

      Volume: 69 Issue: 1 Pages: 61-69

    • DOI

      10.11477/mf.1416200637

    • ISSN
      1344-8129, 1881-6096
    • Year and Date
      2017-01-01
    • Data Source
      KAKENHI-PROJECT-25713034, KAKENHI-PROJECT-15K15339
  • [Journal Article] Aberrant Myokine Signaling in Congenital Myotonic Dystrophy2017

    • Author(s)
      Nakamori Masayuki、Hamanaka Kohei、Thomas James D.、Wang Eric T.、Hayashi Yukiko K.、Takahashi Masanori P.、Swanson Maurice S.、Nishino Ichizo、Mochizuki Hideki
    • Journal Title

      Cell Rep

      Volume: 21 Issue: 5 Pages: 1240-1252

    • DOI

      10.1016/j.celrep.2017.10.018

    • Peer Reviewed / Open Access / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-15K15339, KAKENHI-PROJECT-17H06112, KAKENHI-PROJECT-16H05321
  • [Journal Article] Myotonic dystrophy type 1 patient-derived iPSCs for the investigation of CTG repeat instability.2017

    • Author(s)
      Ueki J, Nakamori M, Nakamura M, Nishikawa M, Yoshida Y, Tanaka A, Morizane A, Kamon M, Araki T, Takahashi MP, Watanabe A, Inagaki N, Sakurai H.
    • Journal Title

      Sci Rep.

      Volume: 13 Issue: 1 Pages: 42522-42522

    • DOI

      10.1038/srep42522

    • Peer Reviewed / Open Access
    • Data Source
      KAKENHI-PROJECT-16H05326, KAKENHI-PROJECT-15J04853, KAKENHI-PROJECT-25713034, KAKENHI-PROJECT-26430053, KAKENHI-PROJECT-15K15339, KAKENHI-PROJECT-15K21113, KAKENHI-PROJECT-17K16711, KAKENHI-PROJECT-16H05321
  • [Journal Article] Myotonic Dystrophy: Advances in Translational Research2017

    • Author(s)
      Nakamori M, Takahashi MP.
    • Journal Title

      Brain Nerve

      Volume: 69 Pages: 61-69

    • NAID

      40021086879

    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Journal Article] パーキンソン病の新展開ー核酸治療2017

    • Author(s)
      中森雅之, 望月秀樹
    • Journal Title

      医学のあゆみ

      Volume: 262 Pages: 683-687

    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Journal Article] Renal dysfunction can be a common complication in patients with myotonic dystrophy 1.2016

    • Author(s)
      Matsumura T, Saito T, Yonemoto N, Nakamori M, Sugiura T, Nakamori A, et al.
    • Journal Title

      J Neurol Sci

      Volume: 368 Pages: 266-71

    • DOI

      10.1016/j.jns.2016.07.036

    • Peer Reviewed
    • Data Source
      KAKENHI-PROJECT-25713034, KAKENHI-PROJECT-15K15339, KAKENHI-PROJECT-16H05321
  • [Journal Article] Splicing misregulation of SCN5A contributes to cardiac-conduction delay and heart arrhythmia in myotonic dystrophy.2016

    • Author(s)
      Freyermuth F, Rau F, Kokunai Y, Linke T, Sellier C, Nakamori M, Kino Y,.......Zimmer T, Furling D, Takahashi MP, Charlet-Berguerand N.
    • Journal Title

      Nat Commun.

      Volume: 7 Issue: 1 Pages: 11067-11067

    • DOI

      10.1038/ncomms11067

    • Peer Reviewed / Acknowledgement Compliant / Open Access / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-15K09314, KAKENHI-PROJECT-25460406, KAKENHI-PROJECT-25461053, KAKENHI-PROJECT-15K15339, KAKENHI-PROJECT-15H04818, KAKENHI-PROJECT-25461106, KAKENHI-PROJECT-25253066, KAKENHI-PROJECT-25713034, KAKENHI-PUBLICLY-15H01567, KAKENHI-PUBLICLY-16H01345, KAKENHI-PROJECT-15H01801, KAKENHI-PROJECT-16H05238, KAKENHI-PROJECT-15K15342, KAKENHI-PROJECT-16K09431
  • [Journal Article] 筋強直性ジストロフィー治療薬開発の現状と患者登録2016

    • Author(s)
      中森雅之, 高橋正紀
    • Journal Title

      難病と在宅ケア

      Volume: 22 Pages: 9-9

    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Journal Article] 筋強直性ジストロフィーの治療戦略2016

    • Author(s)
      中森雅之, 高橋正紀
    • Journal Title

      医学のあゆみ

      Volume: 259 Pages: 58-64

    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Journal Article] 筋強直性ジストロフィーの新規治療開発の動向と標準的医療の意義2016

    • Author(s)
      中森雅之, 高橋正紀
    • Journal Title

      神経内科

      Volume: 85 Pages: 240-246

    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Journal Article] 筋強直性ジストロフィー治療薬開発の現状と患者登録.2016

    • Author(s)
      中森雅之, 高橋正紀
    • Journal Title

      難病と在宅ケア

      Volume: 22 Pages: 9-9

    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Journal Article] 筋強直性ジストロフィーの治療戦略2016

    • Author(s)
      中森雅之, 高橋正紀
    • Journal Title

      医学のあゆみ

      Volume: 259 Pages: 58-64

    • Data Source
      KAKENHI-PROJECT-25713034
  • [Journal Article] 筋強直性ジストロフィーの治療戦略2016

    • Author(s)
      中森雅之, 高橋正紀
    • Journal Title

      医学のあゆみ

      Volume: 259 Pages: 58-64

    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Journal Article] Oral administration of erythromycin decreases RNA toxicity in myotonic dystrophy.2016

    • Author(s)
      Nakamori M, Taylor K, Mochizuki H, Sobczak K, Takahashi MP.
    • Journal Title

      Ann Clin Transl Neurol.

      Volume: 3 Issue: 1 Pages: 42-54

    • DOI

      10.1002/acn3.271

    • Peer Reviewed / Acknowledgement Compliant / Open Access / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-15K15339, KAKENHI-PROJECT-25713034
  • [Journal Article] 筋強直性ジストロフィーの新規治療開発の動向と標準的医療の意義2016

    • Author(s)
      中森雅之, 高橋正紀
    • Journal Title

      神経内科

      Volume: 85 Pages: 240-6

    • Data Source
      KAKENHI-PROJECT-25713034
  • [Journal Article] 筋強直性ジストロフィーの新規治療開発の動向と標準的医療の意義2016

    • Author(s)
      中森雅之, 高橋正紀.
    • Journal Title

      神経内科

      Volume: 85 Pages: 240-6

    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Journal Article] 筋強直性ジストロフィー治療薬開発の現状と患者登録2016

    • Author(s)
      中森雅之, 高橋正紀
    • Journal Title

      難病と在宅ケア

      Volume: 22 Pages: 9-9

    • Data Source
      KAKENHI-PROJECT-25713034
  • [Journal Article] 神経変性疾患のRNA創薬は5年以内に成功するか2015

    • Author(s)
      中森雅之, 望月秀樹
    • Journal Title

      Frontiers in Parkinson Disease.

      Volume: 8 Pages: 141-3

    • Data Source
      KAKENHI-PROJECT-25713034
  • [Journal Article] Biological Efficacy and Toxicity of Diamidines in Myotonic Dystrophy Type 1 Models.2015

    • Author(s)
      Siboni RB, Bodner MJ, Khalifa MM, Docter AG, Choi JY, Nakamori M, Haley MM, Berglund JA.
    • Journal Title

      J Med Chem.

      Volume: 58 Issue: 15 Pages: 5770-80

    • DOI

      10.1021/acs.jmedchem.5b00356

    • Peer Reviewed / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-15K15339, KAKENHI-PROJECT-25713034
  • [Journal Article] Actinomycin D Specifically Reduces Expanded CUG Repeat RNA in Myotonic Dystrophy Models.2015

    • Author(s)
      Siboni RB, Nakamori M, Wagner SD, Struck AJ, Coonrod LA, Harriott SA, Cass DM, Tanner MK, Berglund JA.
    • Journal Title

      Cell Rep.

      Volume: 13 Issue: 11 Pages: 2386-94

    • DOI

      10.1016/j.celrep.2015.11.028

    • Peer Reviewed / Open Access / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-15K15339, KAKENHI-PROJECT-25713034
  • [Journal Article] Large expansion of CTG*CAG repeats is exacerbated by MutSbeta in human cells.2015

    • Author(s)
      Nakatani R, Nakamori M, Fujimura H, Mochizuki H, Takahashi MP.
    • Journal Title

      Sci Rep.

      Volume: 5 Issue: 1 Pages: 11020-11020

    • DOI

      10.1038/srep11020

    • Peer Reviewed / Open Access
    • Data Source
      KAKENHI-PROJECT-15K15339, KAKENHI-PROJECT-25713034
  • [Journal Article] Lomofungin and dilomofungin: inhibitors of MBNL1-CUG RNA binding with distinct cellular effects.2014

    • Author(s)
      Hoskins JW, Ofori LO, Chen CZ, Kumar A, Sobczak K, Nakamori M, Southall N, Patnaik S, Marugan JJ, Zheng W, Austin CP, Disney MD, Miller BL, Thornton CA.
    • Journal Title

      Nucleic Acids Res

      Volume: 42 Issue: 10 Pages: 6591-602

    • DOI

      10.1093/nar/gku275

    • Peer Reviewed / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Journal Article] 筋強直性ジストロフィーにおける筋強直、心臓伝導障害とイオンチャネル異常2014

    • Author(s)
      久保田智哉、中森雅之、高橋正紀
    • Journal Title

      臨床病理

      Volume: 62 Pages: 246-254

    • Data Source
      KAKENHI-PROJECT-25713034
  • [Journal Article] A simple questionnaire for screening patients with myotonic dystrophy type 1.2014

    • Author(s)
      Matsumura T, Kimura T, Kokunai Y, Nakamori M, Ogata K, Fujimura H, Takahashi MP, Mochizuki H, and Sakoda S.
    • Journal Title

      Neurology and Clinical Neuroscience

      Volume: 2 Pages: 97-103

    • Peer Reviewed
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Journal Article] 筋強直性ジストロフィーの治療開発2014

    • Author(s)
      高橋正紀, 中森雅之, 望月秀樹.
    • Journal Title

      臨床神経

      Volume: 54 Pages: 1077-79

    • Data Source
      KAKENHI-PROJECT-25713034
  • [Journal Article] A Kir3.4 mutation causes Andersen–Tawil syndrome by an inhibitory effect on Kir2.1.2014

    • Author(s)
      Kokunai Y, Nakata T, Furuta M, Sakata S, Kimura H, Aiba T, Yoshinaga M, Osaki Y, Nakamori M, Itoh H, Sato T, Kubota T, Kadota K, Shindo K, Mochizuki H, Shimizu W, Horie M, Okamura Y, Ohno K, Takahashi MP
    • Journal Title

      Neurology

      Volume: 82 Issue: 12 Pages: 1058-64

    • DOI

      10.1212/wnl.0000000000000239

    • Peer Reviewed / Open Access
    • Data Source
      KAKENHI-PROJECT-23591245, KAKENHI-PROJECT-24390221, KAKENHI-PROJECT-24591086, KAKENHI-PROJECT-25253016, KAKENHI-PROJECT-25460406, KAKENHI-PROJECT-25860163, KAKENHI-PROJECT-25713034
  • [Journal Article] Reducing levels of toxic RNA with small molecules.2013

    • Author(s)
      Coonrod LA, Nakamori M, Wang W, Carrell S, Hilton CL, Bodner MJ, Siboni RB, Docter AG, Haley MM, Thornton CA, Berglund JA.
    • Journal Title

      ACS Chemical Biology

      Volume: 8 Issue: 11 Pages: 2528-37

    • DOI

      10.1021/cb400431f

    • Peer Reviewed
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Journal Article] Splicing biomarkers of disease severity in myotonic dystrophy.2013

    • Author(s)
      Nakamori M, Sobczak K, Puwanant A, Welle S, Eichinger K, Pandya S, Dekdebrun J, Heatwole CR, McDermott MP, Chen T, Cline M, Tawil R, Osborne RJ, Wheeler TM, Swanson MS, Moxley RT 3rd, Thornton CA.
    • Journal Title

      Annals of Neurology

      Volume: 74 Issue: 6 Pages: 862-72

    • DOI

      10.1002/ana.23992

    • Peer Reviewed
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Journal Article] Detection of slipped-DNAs at the trinucleotide repeats of the myotonic dystrophy type I disease locus in patient tissues.2013

    • Author(s)
      Axford MM, Wang YH, Nakamori M, Zannis-Hadjopoulos M, Thornton CA, Pearson CE.
    • Journal Title

      PLoS Genetics

      Volume: 9 Issue: 12 Pages: e1003866-e1003866

    • DOI

      10.1371/journal.pgen.1003866

    • Peer Reviewed
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Journal Article] 核スプライシング障害とトリプレットリピート病2013

    • Author(s)
      中森雅之, 高橋正紀.
    • Journal Title

      脳21

      Volume: 16 Pages: 71-77

    • Data Source
      KAKENHI-PROJECT-25713034
  • [Patent] 筋強直性ジストロフィー治療薬2016

    • Inventor(s)
      中森雅之
    • Industrial Property Rights Holder
      中森雅之
    • Industrial Property Rights Type
      特許
    • Filing Date
      2016-07-07
    • Overseas
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Patent] 筋強直性ジストロフィー治療薬2016

    • Inventor(s)
      中森雅之
    • Industrial Property Rights Holder
      中森雅之
    • Industrial Property Rights Type
      特許
    • Filing Date
      2016-07-07
    • Overseas
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Patent] 筋強直性ジストロフィー治療薬2016

    • Inventor(s)
      中森雅之
    • Industrial Property Rights Holder
      中森雅之
    • Industrial Property Rights Type
      特許
    • Filing Date
      2016
    • Overseas
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Patent] 筋強直性ジストロフィー治療薬2015

    • Inventor(s)
      中森雅之
    • Industrial Property Rights Holder
      中森雅之
    • Industrial Property Rights Type
      特許
    • Industrial Property Number
      2015-140599
    • Filing Date
      2015-07-14
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Patent] 筋強直性ジストロフィー治療薬2015

    • Inventor(s)
      中森雅之
    • Industrial Property Rights Holder
      中森雅之
    • Industrial Property Rights Type
      特許
    • Industrial Property Number
      2015-140599
    • Filing Date
      2015-07-14
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Patent] Methods of Treating Diseases Associated with Repeat Instability

    • Inventor(s)
      中谷和彦、中森雅之、Christopher Pearson
    • Industrial Property Rights Holder
      国立大学法人大阪大学、ザ・ホスピタル・フォー・シック・チルドレン
    • Overseas
    • Data Source
      KAKENHI-PROJECT-26000007
  • [Presentation] 筋強直性ジストロフィーの治療法開発2023

    • Author(s)
      中森雅之
    • Organizer
      第41回日本神経治療学会学術集会
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] トリプレットリピート病におけるRNA毒性2023

    • Author(s)
      中森雅之
    • Organizer
      第64回日本神経病理学会総会/第66回日本神経化学会大会合同大会
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] エリスロマイシンによる筋強直性ジストロフィー治療2023

    • Author(s)
      中森雅之
    • Organizer
      第44 回日本臨床薬理学会学術総会
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] シヌクレインを標的としたシヌクレイノパチーの早期治療2022

    • Author(s)
      中森雅之
    • Organizer
      第22回日本早期認知症学会学術大会
    • Data Source
      KAKENHI-PROJECT-23K21411
  • [Presentation] Cell type-specific abnormalities of central nervous system in myotonic dystrophy type 1.2022

    • Author(s)
      Nakamori Masayuki
    • Organizer
      13th International Myotonic Dystrophy Consortium Meeting
    • Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-23K21411
  • [Presentation] Cell type-specific abnormalities of central nervous system in myotonic dystrophy type 12022

    • Author(s)
      Masayuki Nakamori
    • Organizer
      13th International Myotonic Dystrophy Consortium Meeting
    • Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] シヌクレインを標的としたシヌクレイノパチーの早期治療2022

    • Author(s)
      中森雅之
    • Organizer
      第22回日本早期認知症学会学術大会
    • Invited
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] 筋強直性ジストロフィーの中枢神経病態2021

    • Author(s)
      中森雅之
    • Organizer
      第40回日本認知症学会学術大会
    • Data Source
      KAKENHI-PROJECT-23K21411
  • [Presentation] 筋強直性ジストロフィーの病態解明と治療開発2021

    • Author(s)
      中森雅之
    • Organizer
      第62回日本神経学会学術大会
    • Invited
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] 筋強直性ジストロフィーの治療開発―基礎研究から臨床試験へ2021

    • Author(s)
      中森雅之
    • Organizer
      第62回日本神経学会学術大会
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] 筋ジストロフィー基盤整備「治験」~筋強直性ジストロフィー患者に対するMYD-0124治験~2021

    • Author(s)
      中森雅之
    • Organizer
      第8回筋ジストロフィー医療研究会
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] 筋強直性ジストロフィーの病態解明と治療開発2021

    • Author(s)
      中森雅之
    • Organizer
      第62回日本神経学会学術大会
    • Invited
    • Data Source
      KAKENHI-PROJECT-23K21411
  • [Presentation] 筋ジストロフィー基盤整備「治験」~筋強直性ジストロフィー患者に対するMYD-0124治験~2021

    • Author(s)
      中森雅之
    • Organizer
      第8回筋ジストロフィー医療研究会
    • Data Source
      KAKENHI-PROJECT-23K21411
  • [Presentation] Ongoing Trials in Myotonic Dystrophy2021

    • Author(s)
      Masayuki Nakamori
    • Organizer
      19th Asian-Oceanian Myology Center Meeting (AOMC 2021)
    • Invited / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] 筋強直性ジストロフィーの中枢神経病態2021

    • Author(s)
      中森雅之
    • Organizer
      第40回日本認知症学会学術大会
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] 筋強直性ジストロフィーの治療開発―基礎研究から臨床試験へ2021

    • Author(s)
      中森雅之
    • Organizer
      第62回日本神経学会学術大会
    • Data Source
      KAKENHI-PROJECT-23K21411
  • [Presentation] Ongoing Trials in Myotonic Dystrophy2021

    • Author(s)
      Masayuki Nakamori
    • Organizer
      19th Asian-Oceanian Myology Center Meeting (AOMC 2021)
    • Invited / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-23K21411
  • [Presentation] Biomarker development and therapeutic target discovery in myotonic dystrophy2020

    • Author(s)
      Masayuki Nakamori
    • Organizer
      第43回日本神経科学大会
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] トリプレットリピート病の革新的遺伝子治療2020

    • Author(s)
      中森雅之
    • Organizer
      日本人類遺伝学会第65回大会
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] ハンチントン病に対する新規低分子治療開発2020

    • Author(s)
      中森雅之
    • Organizer
      第38回日本神経治療学会学術集会
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] Slipped-CAG DNA binding small molecule induces trinucleotide repeat contractions in vivo2020

    • Author(s)
      Masayuki Nakamori
    • Organizer
      第61回日本神経学会学術大会
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] 核酸標的低分子によるリピート病の治療2020

    • Author(s)
      中森雅之
    • Organizer
      第6回日本筋学会学術集会
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] トリプレットリピート病の革新的遺伝子治療2020

    • Author(s)
      中森雅之
    • Organizer
      日本人類遺伝学会第65回大会
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] Slipped-CAG DNA binding small molecule induces trinucleotide repeat contractions in vivo.2020

    • Author(s)
      Nakamori M, Panigrahi G, Lanni S, Hayakawa H, Gall-Duncan T, Eichler E, et al.
    • Organizer
      第61回日本神経学会学術大会
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] シヌクレインを標的としたパーキンソン病治療の現状と展望2020

    • Author(s)
      中森雅之
    • Organizer
      第38回日本神経治療学会学術集会
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] Biomarker development and therapeutic target discovery in myotonic dystrophy2020

    • Author(s)
      中森雅之
    • Organizer
      第43回日本神経科学大会
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] Disease-modifying therapeutics targeting alpha-synuclein.2020

    • Author(s)
      Masayuki Nakamori
    • Organizer
      第61回日本神経学会学術大会
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] 筋強直性ジストロフィーの治療開発と今後の展望2020

    • Author(s)
      中森雅之
    • Organizer
      第74回国立病院総合医学会
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] 筋強直性ジストロフィーの治療法開発2020

    • Author(s)
      中森雅之
    • Organizer
      第38回日本神経治療学会学術集会
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] 筋強直性ジストロフィーの治療法開発2020

    • Author(s)
      中森雅之
    • Organizer
      第38回日本神経治療学会学術集会
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] 筋強直性ジストロフィーの治療開発と今後の展望2020

    • Author(s)
      中森雅之
    • Organizer
      第74回国立病院総合医学会
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] 核酸標的低分子によるリピート病の治療2020

    • Author(s)
      中森雅之
    • Organizer
      第6回日本筋学会学術集会
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] 筋強直性ジストロフィーの異常RNA病態と治療開発2019

    • Author(s)
      中森雅之
    • Organizer
      日本人類遺伝学会第64回大会
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] エリスロマイシンによる筋強直性ジストロフィー治験-第一報2019

    • Author(s)
      中森雅之
    • Organizer
      第37回日本神経治療学会学術集会
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] 筋強直性ジストロフィーの治療開発2019

    • Author(s)
      中森雅之
    • Organizer
      第61回日本小児神経学会学術集会
    • Invited
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] 筋強直性ジストロフィーの異常RNA病態と治療開発2019

    • Author(s)
      中森雅之
    • Organizer
      日本人類遺伝学会第64回大会
    • Invited
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] Slipped-CAG DNA binding small molecule induces trinucleotide repeat contractions in vivo.2019

    • Author(s)
      Nakamori M
    • Organizer
      12th International Myotonic Dystrophy Consortium Meeting
    • Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] シヌクレイノパチーの次世代治療2019

    • Author(s)
      中森雅之
    • Organizer
      第37回日本神経治療学会学術集会
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] Slipped-CAG DNA binding small molecule induces trinucleotide repeat contractions in vivo.2019

    • Author(s)
      Nakamori M.
    • Organizer
      12th International Myotonic Dystrophy Consortium Meeting
    • Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] 筋強直性ジストロフィーに対するエリスロマイシン治療2019

    • Author(s)
      中森雅之
    • Organizer
      第6回筋ジストロフィー医療研究会
    • Invited
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] 核酸医薬によるシヌクレイノパチーの治療開発2019

    • Author(s)
      中森雅之
    • Organizer
      第38回日本認知症学会学術集会
    • Invited
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] シヌクレイノパチーの次世代治療2019

    • Author(s)
      中森雅之
    • Organizer
      第37回日本神経治療学会学術集会
    • Invited
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] 筋強直性ジストロフィーの治療開発2019

    • Author(s)
      中森雅之
    • Organizer
      第61回日本小児神経学会学術集会
    • Invited
    • Data Source
      KAKENHI-PROJECT-19K22597
  • [Presentation] 筋強直性ジストロフィーに対するエリスロマイシン治療2019

    • Author(s)
      中森雅之
    • Organizer
      第6回筋ジストロフィー医療研究会
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] 核酸医薬によるシヌクレイノパチーの治療開発2019

    • Author(s)
      中森雅之
    • Organizer
      第38回日本認知症学会学術集会
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] Aberrant interleukin-6 signaling in myotonic dystrophy2018

    • Author(s)
      Nakamori, M
    • Organizer
      第59回日本神経学会学術大会
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] Development of Isoquinoline Ligand Binding to r(CUG) Repeats2018

    • Author(s)
      Jun Matsumoto, Jinxing Li, Masayuki Nakamori, Asako Murata, Chikara Dohno, Kazuhiko Nakatani
    • Organizer
      International Symposium on Nucleic Acids Chemistry (ISNAC) 2018
    • Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-26000007
  • [Presentation] Oral administration of erythromycin decreases RNA toxicity in myotonic dystrophy.2018

    • Author(s)
      Nakamori, M
    • Organizer
      New Directions in Biology and Disease of Skeletal Muscle Conference
    • Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] Oral administration of erythromycin decreases RNA toxicity in myotonic dystrophy2018

    • Author(s)
      Nakamori, M
    • Organizer
      New Directions in Biology and Disease of Skeletal Muscle Conference
    • Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] Antisense oligonucleotide therapeutics for neurological and neuromuscular disorders.2018

    • Author(s)
      Nakamori, M
    • Organizer
      East Asia Neurology Forum 2018
    • Invited / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] Antisense oligonucleotide therapeutics for neurological and neuromuscular disorders2018

    • Author(s)
      Nakamori, M
    • Organizer
      East Asia Neurology Forum 2018
    • Invited / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] 筋強直性ジストロフィーとマイオカインシグナル異常2018

    • Author(s)
      中森雅之
    • Organizer
      日本筋学会第4回学術集会
    • Invited
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] 筋強直性ジストロフィーとマイオカインシグナル異常2018

    • Author(s)
      中森雅之
    • Organizer
      日本筋学会第4回学術集会
    • Invited
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] 筋強直性ジストロフィーの病態解明と治療開発研究―先天性筋強直性ジストロフィーにおけるマイオカインシグナル異常2018

    • Author(s)
      中森雅之
    • Organizer
      平成29年度精神・神経疾患研究開発費 筋ジストロフィー合同班会議
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] Aberrant interleukin-6 signaling in myotonic dystrophy2018

    • Author(s)
      Nakamori, M
    • Organizer
      第59回日本神経学会学術大会
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] リピート病におけるリピート伸長機構解明とその制御による治療法開発2017

    • Author(s)
      中森雅之
    • Organizer
      2017年度生命科学系学会合同年次大会
    • Invited
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] Phenotype-genotype/epigenotype correlation and aberrant inflammatory signaling in congenital myotonic dystrophy2017

    • Author(s)
      Nakamori M
    • Organizer
      11th International Myotonic Dystrophy Consortium Meeting
    • Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] エリスロマイシンによる筋強直性ジストロフィーの治療2017

    • Author(s)
      中森雅之
    • Organizer
      第35回日本神経治療学会総会
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] 筋強直性ジストロフィーの病態と治療法開発2017

    • Author(s)
      中森雅之
    • Organizer
      第3回日本筋学会学術集会
    • Invited
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] PHENOTYPE-GENOTYPE/EPIGENOTYPE CORRELATION IN CONGENITAL MYOTONIC DYSTROPHY2017

    • Author(s)
      Nakamori M
    • Organizer
      XXIII World Congress of Neurology
    • Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] 核酸医薬におけるパーキンソン病の革新的治療法の開発2017

    • Author(s)
      中森雅之
    • Organizer
      第17回日本抗加齢医学会総会
    • Invited
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] リピート病におけるリピート伸長機構解明とその制御による治療法開発2017

    • Author(s)
      中森雅之
    • Organizer
      2017年度生命科学系学会合同年次大会
    • Invited
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] 筋強直性ジストロフィーの病態解明と治療開発研究2017

    • Author(s)
      中森雅之
    • Organizer
      平成28年度 精神・神経疾患研究開発費 筋ジストロフィー合同班会議
    • Place of Presentation
      東京
    • Invited
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] Phenotype-genotype/epigenotype correlation and aberrant inflammatory signaling in congenital myotonic dystrophy.2017

    • Author(s)
      Nakamori, M
    • Organizer
      11th International Myotonic Dystrophy Consortium Meeting
    • Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] 筋強直性ジストロフィーの病態と治療法開発2017

    • Author(s)
      中森雅之
    • Organizer
      第3回日本筋学会学術集会
    • Invited
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] エリスロマイシンによる筋強直性ジストロフィーの治療2017

    • Author(s)
      中森雅之
    • Organizer
      第35回日本神経治療学会総会
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] 核酸医薬におけるパーキンソン病の革新的治療法の開発2017

    • Author(s)
      中森雅之
    • Organizer
      第17回日本抗加齢医学会総会
    • Invited
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] Gene therapy with antisense oligonucleotides for neurological and neuromuscular disorders.2016

    • Author(s)
      Nakamori M
    • Organizer
      第57回日本神経学会学術大会
    • Place of Presentation
      神戸
    • Invited
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] ハンチントン病の将来の治療2016

    • Author(s)
      中森雅之
    • Organizer
      第10回 パーキンソン病・運動障害疾患コングレス
    • Place of Presentation
      京都
    • Invited
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] ハンチントン病の将来の治療2016

    • Author(s)
      中森雅之
    • Organizer
      第10回 パーキンソン病・運動障害疾患コングレス
    • Place of Presentation
      京都
    • Invited
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] Antisense oligonucleotides therapy for neurological and neuromuscular disorders.2016

    • Author(s)
      Nakamori M
    • Organizer
      第22回日本遺伝子細胞治療学会学術集会
    • Place of Presentation
      東京
    • Invited
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] Oral administration of erythromycin decreases RNA toxicity in myotonic dystrophy.2016

    • Author(s)
      Nakamori M
    • Organizer
      第57回日本神経学会学術大会
    • Place of Presentation
      神戸
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] Gene therapy with antisense oligonucleotides for neurological and neuromuscular disorders2016

    • Author(s)
      Nakamori M
    • Organizer
      第57回日本神経学会学術大会
    • Invited
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] Antisense oligonucleotides therapy for neurological and neuromuscular disorders.2016

    • Author(s)
      Nakamori M
    • Organizer
      第22回日本遺伝子細胞治療学会学術集会
    • Place of Presentation
      東京
    • Invited
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] Gene therapy with antisense oligonucleotides for neurological and neuromuscular disorders.2016

    • Author(s)
      Nakamori M
    • Organizer
      第57回日本神経学会学術大会
    • Place of Presentation
      神戸
    • Invited
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] Oral administration of erythromycin decreases RNA toxicity in myotonic dystrophy.2016

    • Author(s)
      Nakamori M
    • Organizer
      第57回日本神経学会学術大会
    • Place of Presentation
      神戸
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] 筋強直性ジストロフィーの新しい治療2016

    • Author(s)
      中森雅之
    • Organizer
      第4回北海道東北筋強直性ジストロフィー臨床研究会
    • Place of Presentation
      旭川
    • Invited
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] 筋強直性ジストロフィーの新しい治療2016

    • Author(s)
      中森雅之
    • Organizer
      第4回北海道東北筋強直性ジストロフィー臨床研究会
    • Place of Presentation
      旭川
    • Invited
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] Antisense oligonucleotides therapy for neurological and neuromuscular disorders2016

    • Author(s)
      Nakamori M
    • Organizer
      第22回日本遺伝子細胞治療学会学術集会
    • Invited
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] Oral administration of erythromycin decreases RNA toxicity in myotonic dystrophy2016

    • Author(s)
      Nakamori M
    • Organizer
      第57回日本神経学会学術大会
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] ハンチントン病の将来の治療2016

    • Author(s)
      中森雅之
    • Organizer
      第10回 パーキンソン病・運動障害疾患コングレス
    • Invited
    • Data Source
      KAKENHI-PROJECT-16H05321
  • [Presentation] Myotonic dystrophy: toxic RNA and spliceopathy.2015

    • Author(s)
      Nakamori M
    • Organizer
      第58回日本神経化学会大会
    • Place of Presentation
      埼玉
    • Invited
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] Phenotype-genotype correlation in congenital myotonic dystrophy.2015

    • Author(s)
      Nakamori M
    • Organizer
      10th Brain Research Conference: RNA Metabolism in Neurological Disease
    • Place of Presentation
      Chicago, U.S.A.
    • Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] 先天性筋強直性ジストロフィー症の筋未熟性とCpGメチル化異常.2015

    • Author(s)
      中森雅之
    • Organizer
      第56回日本神経学会学術大会
    • Place of Presentation
      朱鷺メッセ、新潟
    • Year and Date
      2015-05-22
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] Phenotype-genotype correlation in congenital myotonic dystrophy.2015

    • Author(s)
      Nakamori M
    • Organizer
      10th Brain Research Conference: RNA Metabolism in Neurological Disease
    • Place of Presentation
      Chicago, IL, U.S.A.
    • Year and Date
      2015-10-16
    • Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] Modeling genetic instability of the CTG repeats in Myotonic Dystrophy type 1 (DM1) patient-derived iPS cell2015

    • Author(s)
      Junko UEKI, Masayuki NAKAMORI, Masanori TAKAHASHI, Hidetoshi SAKURAI
    • Organizer
      The 10th International Myotonic Dystrophy Consortium Meeting
    • Place of Presentation
      PARIS, FRANCE
    • Year and Date
      2015-06-08
    • Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-26430053
  • [Presentation] Aberrant methylation of the CTCF binding site is associated with antisense transcription and disease severity in congenital myotonic dystrophy.2015

    • Author(s)
      Nakamori M
    • Organizer
      10th International Myotonic Dystrophy Consortium Meeting
    • Place of Presentation
      Paris, France.
    • Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] Aberrant methylation of the CTCF binding site is associated with antisense transcription and disease severity in congenital myotonic dystrophy.2015

    • Author(s)
      Nakamori M
    • Organizer
      10th International Myotonic Dystrophy Consortium Meeting
    • Place of Presentation
      Paris, France
    • Year and Date
      2015-06-10
    • Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] 先天性筋強直性ジストロフィー症の筋未熟性とCpGメチル化異常2015

    • Author(s)
      中森雅之
    • Organizer
      第56回日本神経学会学術大会
    • Place of Presentation
      新潟
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] 筋強直性ジストロフィーの治療戦略2015

    • Author(s)
      中森雅之
    • Organizer
      第2回筋ジストロフィー医療研究会
    • Place of Presentation
      大阪
    • Invited
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] Myotonic dystrophy; toxic RNA and spliceopathy.2015

    • Author(s)
      Nakamori M
    • Organizer
      第58回日本神経化学会大会
    • Place of Presentation
      大宮ソニックシティ、埼玉
    • Year and Date
      2015-09-11
    • Invited
    • Data Source
      KAKENHI-PROJECT-15K15339
  • [Presentation] Phenotype-genotype correlation in congenital myotonic dystrophy.2015

    • Author(s)
      Nakamori M.
    • Organizer
      The 8th International Conference on Unstable Microsatellites and Human Disease
    • Place of Presentation
      Guanacaste, Costa Rica
    • Year and Date
      2015-01-18
    • Invited / Int'l Joint Research
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] 筋強直性ジストロフィーにおけるスプライシングバイオマーカーの確立2014

    • Author(s)
      中森雅之
    • Organizer
      第55回日本神経学会学術大会
    • Place of Presentation
      福岡
    • Year and Date
      2014-05-22
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] 筋強直性ジストロフィーにおける網羅的スプライシング解析とスプライシングバイオマーカーの確立2014

    • Author(s)
      中森雅之
    • Organizer
      日本人類遺伝学会 第59回大会
    • Place of Presentation
      東京
    • Year and Date
      2014-11-21
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] Phenotype-genotype correlation in congenital myotonic dystrophy.2013

    • Author(s)
      Masayuki Nakamori
    • Organizer
      8th Brain Research Conference
    • Place of Presentation
      San Diego (U.S.A.)
    • Year and Date
      2013-11-07
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] トリプレットリピート病におけるリピート長の制御2013

    • Author(s)
      中森雅之
    • Organizer
      第54回日本神経学会学術大会
    • Place of Presentation
      東京
    • Data Source
      KAKENHI-PROJECT-24890110
  • [Presentation] 筋強直性ジストロフィーの治療戦略2013

    • Author(s)
      中森雅之
    • Organizer
      平成24年度筋ジストロフィー合同班会議
    • Place of Presentation
      東京
    • Data Source
      KAKENHI-PROJECT-24890110
  • [Presentation] Pentamidine and analogs as inhibitors of transcription.2013

    • Author(s)
      Coonrod L, Nakamori M
    • Organizer
      9th International Myotonic Dystrophy Consortium Meeting
    • Place of Presentation
      Donostia San Sebastian (Spain)
    • Year and Date
      2013-10-18
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] トリプレットリピート病におけるリピート長の制御2013

    • Author(s)
      中森雅之
    • Organizer
      第54回日本神経学会学術大会
    • Place of Presentation
      東京国際フォーラム(東京都)
    • Year and Date
      2013-05-30
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] Actinomycin D inhibits transcription of CUG RNA in a DM1 model.2013

    • Author(s)
      Siboni R, Nakamori M
    • Organizer
      9th International Myotonic Dystrophy Consortium Meeting
    • Place of Presentation
      Donostia San Sebastian (Spain)
    • Year and Date
      2013-10-18
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] トリプレットリピート病におけるリピート長伸長機構の解明と制御2013

    • Author(s)
      中森雅之
    • Organizer
      第58回日本人類遺伝学会大会
    • Place of Presentation
      江陽グランドホテル(宮城県)
    • Year and Date
      2013-11-21
    • Data Source
      KAKENHI-PROJECT-25713034
  • [Presentation] Phenotype-genotype correlation in congenital myotonic dystrophy.2013

    • Author(s)
      Masayuki Nakamori
    • Organizer
      9th International Myotonic Dystrophy Consortium Meeting
    • Place of Presentation
      Donostia San Sebastian (Spain)
    • Year and Date
      2013-10-17
    • Data Source
      KAKENHI-PROJECT-25713034
  • 1.  TAKAHASHI Masanori (20359847)
    # of Collaborated Projects: 2 results
    # of Collaborated Products: 4 results
  • 2.  NAKATANI Kazuhiko (70237303)
    # of Collaborated Projects: 1 results
    # of Collaborated Products: 3 results
  • 3.  DOHNO Chikara (60420395)
    # of Collaborated Projects: 1 results
    # of Collaborated Products: 2 results
  • 4.  TAKEI Fumie (30252711)
    # of Collaborated Projects: 1 results
    # of Collaborated Products: 0 results
  • 5.  MURATA Asako (50557121)
    # of Collaborated Projects: 1 results
    # of Collaborated Products: 4 results
  • 6.  SAKURAI Hidetoshi (80528745)
    # of Collaborated Projects: 1 results
    # of Collaborated Products: 1 results
  • 7.  WATANABE Akira (60506765)
    # of Collaborated Projects: 1 results
    # of Collaborated Products: 0 results
  • 8.  AIKAWA Haruo
    # of Collaborated Projects: 1 results
    # of Collaborated Products: 0 results
  • 9.  YAMADA Takeshi
    # of Collaborated Projects: 1 results
    # of Collaborated Products: 0 results
  • 10.  SHIBATA Tomonori
    # of Collaborated Projects: 1 results
    # of Collaborated Products: 0 results
  • 11.  NAGAI Takeharu
    # of Collaborated Projects: 1 results
    # of Collaborated Products: 0 results
  • 12.  UEKI Junko
    # of Collaborated Projects: 1 results
    # of Collaborated Products: 1 results
  • 13.  Jonouchi Tatsuya
    # of Collaborated Projects: 1 results
    # of Collaborated Products: 0 results
  • 14.  SUZUKI Naoki
    # of Collaborated Projects: 0 results
    # of Collaborated Products: 2 results
  • 15.  HIDA Eisuke
    # of Collaborated Projects: 0 results
    # of Collaborated Products: 1 results
  • 16.  SHIMIZU Fumitaka
    # of Collaborated Projects: 0 results
    # of Collaborated Products: 1 results
  • 17.  青木 正志
    # of Collaborated Projects: 0 results
    # of Collaborated Products: 2 results
  • 18.  割田 仁
    # of Collaborated Projects: 0 results
    # of Collaborated Products: 2 results
  • 19.  佐藤 倫治
    # of Collaborated Projects: 0 results
    # of Collaborated Products: 1 results
  • 20.  稲垣 暢也
    # of Collaborated Projects: 0 results
    # of Collaborated Products: 1 results

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